Why Join Us?
Be a hero for our rare disease patients
At Ultragenyx, we fundamentally believe that taking real impactful action to care for the needs of patients and our people is always the right thing to do. To achieve this goal, our vision is to lead the future of rare disease medicine. For us, this means going where other biopharma companies won’t go – challenging the status quo and creating a new model that advances our field so more patients and caregivers can benefit from life-changing treatments. We do this by following the science, applying a novel rapid development approach, making innovative medicines at fair and reasonable prices, and creating a collaborative ecosystem to reach patients in ways that are most meaningful for them.
Our commitment and care for patients extends to our people, so culture is an essential cornerstone for Ultragenyx. We remain continuously focused on creating a supportive and inclusive environment of profound learning and growth – so employees can thrive in all areas of their lives, in and outside of work. Ultimately, we want to be an organization where we would be proud for our family, friends and children to work.
If you want to have a meaningful impact, do the best work of your career, and grow a lot, both professionally and personally, come join our team.
Position Summary:
ultrafocused – Work together to fearlessly uncover new possibilities
The Director, Head of Global Medical Information is responsible for setting the strategic direction, operational excellence, and scientific rigor of Ultragenyx’s global medical information function. This leader ensures the accurate, balanced, and timely communication of scientific information to healthcare professionals, patients, and internal stakeholders across Ultragenyx’s rare disease portfolio.
Reporting to the Head of Scientific Communications, the Director oversees both internal team members and external vendor partners, while contributing directly to the development and review of scientific materials. This “player–coach” role is critical to ensuring inspection ready medical information operations, compliant scientific exchange, and seamless alignment with Medical Affairs, Regulatory, Pharmacovigilance, Legal, and Commercial partners.
Work Model:
Remote: Officially documented as working full-time from home, with travel to Ultragenyx's offices or other locations on occasion as needed.
Responsibilities:
Global Medical Information Leadership
- Lead the global medical information strategy and operations, ensuring compliant, evidence based responses to unsolicited inquiries from HCPs, patients, and internal teams.
- Oversee creation, review, and maintenance of global standard response letters, FAQs, and medical information resources across marketed and pipeline programs.
- Ensure all materials remain scientifically current, aligned with evolving data, and consistent with regulatory expectations globally.
Inquiry Management & Vendor Oversight
- Provide strategic direction and quality oversight for outsourced medical information contact center operations.
- Define performance standards, service metrics, and quality management processes for vendor partners.
- Ensure clear triage pathways and timely escalation of complex scientific inquiries to internal experts.
- Monitor inquiry trends to identify emerging knowledge gaps, safety issues, or reputational risks.
- Maintain inspection readiness for all medical information systems, processes, and documentation.
Medical Review & Scientific Governance
- Serve as Medical reviewer within the Medical–Legal–Regulatory process for assigned assets.
- Provide scientific review of medical information materials, HCP resources, training content, and other scientific communications.
- Ensure all externally facing materials are accurate, balanced, and aligned with current evidence and regulatory guidance.
- Guide the appropriate handling of off label and unsolicited scientific inquiries.
Scientific Content Strategy
- Govern the scientific accuracy and consistency of all medical information content.
- Partner with Medical Affairs subject matter experts to ensure response materials reflect the company’s scientific narrative.
- Align medical information with publications, field medical materials, and medical education strategies.
- Maintain and govern the MI scientific response library supporting global field medical consistency.
Cross Functional Partnerships
- Represent Medical Information on cross functional product teams for marketed and pipeline assets.
- Collaborate with Pharmacovigilance on identification and triage of safety related information.
- Work closely with Regulatory, Legal, and Compliance to ensure adherence to global guidelines governing scientific exchange.
- Partner with Scientific Communications to ensure coherent scientific messaging across channels.
Insights Generation & Strategic Input
- Analyze inquiry trends to identify emerging scientific questions, evidence gaps, and opportunities to strengthen the scientific narrative.
- Translate insights into actionable recommendations for Medical Affairs, Scientific Communications, and field medical teams.
- Support development of publications, response materials, and educational initiatives informed by inquiry derived insights.
Launch Readiness
- Lead medical information preparations for product launches, including core response materials, anticipated inquiry matrices, and alignment with field medical and Medical Affairs launch plans.
Requirements:
- Advanced degree in life sciences, pharmacy, or medicine (PharmD, PhD, MD, or equivalent), with rare disease experience strongly preferred.
- 10+ years of experience in pharmaceutical or biotechnology industry roles, including at least 7 years of experience in Medical Information.
- Demonstrated experience leading or managing a Medical Information function or major Medical Information program, including oversight of inquiry management processes and scientific response content.
- Experience with medical information databases and inquiry management systems.
- Experience supporting medical review of scientific materials within an MRC process.
- Experience overseeing outsourced Medical Information contact center vendors strongly preferred.
- Experience working cross-functionally with Regulatory, Pharmacovigilance, Legal, and Commercial teams.
- Strong understanding of regulatory requirements governing medical information and scientific exchange.
- Excellent written and verbal scientific communication skills.
- Experience supporting product launches and pipeline programs.
#LI-AL1 #LI-Remote
Full Time employees across the globe enjoy a range of benefits, including, but not limited to:
· Generous vacation time and public holidays observed by the company
· Volunteer days
· Long term incentive and Employee stock purchase plans or equivalent offerings
· Employee wellbeing benefits
· Fitness reimbursement